TY  - JOUR

T1  - Systemic delivery of scAAV9 expressing SMN prolongs survival in a model of spinal muscular atrophy.

JO  - Sci Transl Med

PY  - 2010/06/09

AU  - Valori CF

AU  - Ning K

AU  - Wyles M

AU  - Mead RJ

AU  - Grierson AJ

AU  - Shaw PJ

AU  - Azzouz M

ED  - 

DO  - DOI: 10.1126/scitranslmed.3000830

VL  - 2

IS  - 35

SP  - 35ra42

Y2  - 2024/12/22

ER  -