TY - JOUR T1 - Current and investigational treatments for spinal muscular atrophy JO - Expert Opinion on Orphan Drugs PY - 2014/05/01 AU - Tam JKV AU - Karyka E AU - Azzouz M ED - DO - DOI: 10.1517/21678707.2014.901910 VL - 2 IS - 5 SP - 465 EP - 476 Y2 - 2024/12/22 ER -