TY - JOUR T1 - Systematic review of presymptomatic treatment for spinal muscular atrophy JO - International Journal of Neonatal Screening UR - https://eprints.whiterose.ac.uk/id/eprint/216703 PY - 2024/08/14 AU - Cooper K AU - Nalbant G AU - Sutton A AU - Harnan S AU - Thokala P AU - Chilcott J AU - McNeill A AU - Bessey A ED - DO - DOI: 10.3390/ijns10030056 PB - MDPI AG VL - 10 IS - 3 Y2 - 2024/12/22 ER -