@inproceedings{inproceedings, title = {{PRO15 COST-EFFECTIVENESS OF NUSINERSEN AND ONASEMNOGENE ABEPARVOVEC FOR INFANTILE-ONSET SPINAL MUSCULAR ATROPHY (TYPE I SMA) IN THE US}}, publisher = {{Elsevier BV}}, url = {{}}, year = {{2019}}, month = {{5}}, author = {{Thokala P and Stevenson M and Kumar VM and Ren S and Chapman R and Ellis A and Rind D}}, doi = {{10.1016/j.jval.2019.04.1648}}, volume = {{22}}, journal = {{Value in Health}}, pages = {{S337-S338}}, note = {{Accessed on 2024/10/18}}}