TY - CONF T1 - Investigating the Specificity of RNAi Molecules in Human Gene Therapy for Superoxide Dismutase 1-linked Familial Amyotrophic Lateral Sclerosis JO - HUMAN GENE THERAPY PY - 2016/07/01 AU - Scarrott J AU - Ferraiuolo L AU - Heath P AU - Gelsthorpe C AU - Kaspar B AU - Shaw DP AU - Azzouz M ED - VL - 27 IS - 7 SP - A16 EP - A17 Y2 - 2024/12/22 ER -